Eplontersen trial fails to meet primary endpoint in transthyretin-mediated amyloid cardiomyopathy

The CARDIO-TTRansform trial investigating eplontersen in patients with transthyretin-mediated amyloid cardiomyopathy did not meet its primary efficacy endpoint, according to results presented in a Hot Line session at ESC Congress 2026.

source https://medicalxpress.com/news/2026-08-eplontersen-trial-primary-endpoint-transthyretin.html

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